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- CASGEVY® (exagamglogene autotemcel) | Patient Website
CASGEVY is a one-time therapy used to treat people aged 12 years and older with: sickle cell disease (SCD) who have frequent vaso-occlusive crises or VOCs beta thalassemia (β-thalassemia) who need regular blood transfusions
- Exagamglogene autotemcel - Wikipedia
Exagamglogene autotemcel, sold under the brand name Casgevy, is a gene therapy used for the treatment of sickle cell disease [3] [5] and transfusion-dependent beta thalassemia [3] It was developed by Vertex Pharmaceuticals and CRISPR Therapeutics [9]
- FDA Approves First Gene Therapies to Treat Patients with Sickle Cell . . .
Casgevy, a cell-based gene therapy, is approved for the treatment of sickle cell disease in patients 12 years of age and older with recurrent vaso-occlusive crises Casgevy is the first
- Exagamglogene Autotemcel for Severe Sickle Cell Disease
Exagamglogene autotemcel (exa-cel) is a nonviral cell therapy designed to reactivate fetal hemoglobin synthesis by means of ex vivo clustered regularly interspaced short palindromic repeats
- Casgevy: Uses, Dosage, Side Effects, Warnings - Drugs. com
Casgevy (exagamglogene autotemcel) is a gene therapy that is given as a one-time intravenous infusion to treat adults and children aged 12 years and older with: Sickle cell disease with recurrent vaso-occlusive crises (VOCs) Transfusion-dependent β-thalassemia (TDT)
- Revolutionary breakthrough: FDA approves CASGEVY, the first CRISPR Cas9 . . .
Casgevy, the first FDA-approved CRISPR Cas9 gene therapy for sickle cell disease (SCD), offers a curative approach and eliminates the need for recurrent transfusions and transplants, thereby significantly enhancing the quality of life of individuals with SCD
- CASGEVY® (exagamglogene autotemcel) Mechanism of Action in SCD . . .
Discover CASGEVY (exagamglogene autotemcel): a first-of-its-kind, CRISPR Cas9-modified cellular gene therapy INDICATION CASGEVY is indicated for the treatment of patients aged 12 years and older with: sickle cell disease (SCD) with recurrent vaso-occlusive crises (VOCs) transfusion-dependent β-thalassemia (TDT) IMPORTANT SAFETY INFORMATION
- The worlds 1st CRISPR therapy has been approved. Heres everything you . . .
Exa-cel, also known by its brand name Casgevy, received its first regulatory approval on Nov 16, 2023 from the U K Medicines and Healthcare products Regulatory Agency (MHRA) to treat two
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